Keyphrases
Succinic Semialdehyde Dehydrogenase Deficiency (SSADHD)
100%
GABA Metabolism
100%
Quality of Life Survey
100%
Rare Disorders
100%
Quality of Life
40%
Family Caregivers
40%
Patient's Family
40%
Family Experience
20%
Overall Impact
20%
Family Impact
20%
Clinical Tool
20%
Meaningful Outcomes
20%
Focus Group Discussion
20%
Family Perspectives
20%
Cognitive Function
20%
Intellectual Functioning
20%
Physical Function
20%
Patient Report
20%
Rare Disease Clinical Trial
20%
Psychological Function
20%
Neurodevelopmental Morbidities
20%
Social Function
20%
Behavioral Function
20%
Medicine and Dentistry
Quality of Life
100%
Orphan Disorder
100%
Succinic Semialdehyde Dehydrogenase Deficiency
100%
4 Aminobutyric Acid Metabolism
100%
Rare Disease
20%
Clinical Trial
20%
Nursing and Health Professions
Quality of Life
100%
4 Aminobutyric Acid
100%
Succinate Semialdehyde Dehydrogenase
100%
Diseases
100%
Rare Disease
20%